Gene Therapy Restores Sight for Blind Patients with Hereditary Eye Disease

A groundbreaking treatment for a rare form of hereditary blindness has moved closer to U.S. approval. This week advisers to the Food and Drug Administration recommended the experimental gene therapy, which replaces a defective gene. If the FDA agrees by mid-January, this would become the first gene therapy in the U.S. for an inherited disease. VOA’s Deborah Block tells us how a breakthrough treatment helped restore vision to a teenager who has his sights on a singing career.


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